FDA Approved Clinical Trials
FDA Approved Pharmaceutical Clinical Trials
Clinical trials are underway to study treatments for ASMD and NPC. Follow the links below for information.
ASMD Clinical Trial
NPC Clinical Trials
- Cyclo Therapeutics, Inc.
- Mallinckrodt Pharmaceuticals
- National Institutes of Health
- Niemann-Pick Disease, Recruiting
- Niemann-Pick Disease, Active not Recruiting
- Niemann-Pick Disease, Completed
Questions about Clinical Trial Participation? Visit:
The NNPDF posts new information regarding clinical trial updates as soon as it is received. Please review the following Clinical Trial Update procedure for alerting you to these updates as they are made:
1. The NNPDF office will post information received about trials and expanded access therapies from companies on the NNPDF website under the appropriate pharmaceutical company.
2. When information is received it is:
- Posted on the NNPDF website
- Shared via email announcement
- Summary post is made on the NNPDF Facebook Business page, NNPDF Facebook Awareness Group, NNPDF Facebook Staff page and Twitter with a link back to our website where you can find more detailed information.
3. All updates from pharmaceutical companies are included in the next monthly e-newsletter with links back to the original posting on the website.