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Family Support & Medical Conference
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Niemann-Pick Awareness Month
Rare Disease Day
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Industry Policy Statement
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Approved Treatments
ASMD
Acid Sphingomyelinase Deficiency
Xenpozyme
NPC
Niemann-Pick Disease type C
AQNEURSA
MIPLYFFA
Clinical Trials
Azafaros
Cyclo Therapeutics, Inc.
Mandos Health
National Institutes of Health
Glossary of Terms
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