NPC & ASMD Newborn Screening Webinar Recording
Videos
March 4, 2024
Supporting one another. Supporting our community.
#SuperSibling Series: Serina Heinze
Videos
October 2023 – Niemann-Pick Awareness Month
#SuperSibling: Serina Heinze
Serina kicks off our #SuperSibling series with a incredibly inspirational and heartfelt message. Each week in October we’ll highlight another #SuperSibling from the Niemann-Pick community. Watch Serina’s video message.
#niemannpickawareness #npc #asmd #raredisease
Supporting one another. Supporting our community.
INPDA Webinar: Patient Reported Outcomes – Pediatric Experience with Olipudase alfa
Videos
Slideshow Presentation:Â The impacts of olipudase alfa on pediatric patients with ASMD and their families: Results of an international survey
Supporting one another. Supporting our community.
A Message from Becky McGuire
A Message from Mary Francis Harmon
A Message from Cara Gilmore
AllStripes NPC Sibling Research Study
Overview of Ongoing Clinical Development Programs for Investigational Therapies in NPC and Q&A for Families
