FDA Approved Clinical Trials
FDA Approved Clinical Trials are underway to study treatments for Acid Sphingomyelinase Deficiency (ASMD) and Niemann-Pick Disease type C (NPC). Follow the links below for more information.
Acid Sphingomyelinase Deficiency (ASMD)
RECRUITING:
- Sanofi (Age 0-24 months with ASMD)