This page is dedicated to news and information about IntraBio’s therapies for use in Niemann-Pick Disease Type C (NPC). Information is released as it becomes available.
IntraBio is developing a number of small-molecule drug candidates that have broad applicability to rare and common neurological disorders, genetic, and inflammatory diseases. Their current lead drug candidate, IB1001, is initially being developed to treat three rare, genetic diseases where there are extremely high unmet medical needs: Niemann-Pick disease type C, GM2 Gangliosidosis (Tay-Sachs and Sandhoff Disease), and Ataxia-Telangiectasia (A-T; an inherited Cerebellar Ataxia). Click the link below for additional information.
IntraBio Receives Niemann-Pick Disease Orphan Drug Designation from the FDA for IB1000 Series