NPC & ASMD Clinical Trial & Research Updates
Dear NNPDF Families and Friends,
In tandem with World Rare Disease Day 2015 and in support of our NPD families WORLD-WIDE, the National Niemann-Pick Disease Foundation (NNPDF) is pleased to share the most recent research and clinical trip updates within the Niemann-Pick Disease Community.
The update includes: Cyclodextrin (NPC Pediatric), Vorinostat (NPC Adult) & Enzyme Replacement Therapy (ASMD ~ pediatrics)
The NNPDF also received notification of a recent on-line publication highlighting the work of Charles Vite, Ph.D, and the invaluable work that he has been doing with the naturally-occurring Niemann-Pick Type C felines at the University of Pennsylvania ~ School of Veterinary Medicine.