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Posted by on Mar 11, 2015 in Foundation NewsLine |

Phase 2/3 Adult and Phase 1/2 Pediatric Clinical Trial Update

Dear NNPDF Families and Friends,

Representatives of the National Niemann-Pick Disease Foundation (NNPDF), Niemann-Pick UK and the International Niemann-Pick Disease Alliance (INPDA) today participated in a teleconference with Genzyme, A Sanofi Company.

We were pleased to learn that plans for the Phase 2/3 Adult and Phase 1/2 Pediatric Clinical trial of rhASM for ASMD Niemann-Pick disease continue to progress. Discussions continue with the regulatory authorities, including the FDA and the EMA and we expect Genzyme to release a more detailed community update soon.

Please contact the NNPDF Central Offices should you have any questions at: nnpdf@nnpdf.org